DMD treatment SMT-01, a cell replacement therapy, received FDA orphan drug and rare pediatric disease designations.

For a long time, columnist Robin Stemple resisted using a walker to navigate around his home, but eventually, he had to put ...

Last Saturday, I had the honor of participating in the third Singapore Health Patient Advocate Connection event (SPACe) ...

Losmapimod, an investigational medication from Fulcrum Therapeutics, failed to significantly outperform a placebo at ...

The U.S. Food and Drug Administration granted rare pediatric disease designation to NS-050/NCNP-03, an exon-skipping DMD ...

Atamyo has partnered with the Dion Foundation to expand into the U.S. a clinical trial testing the gene therapy ATA-200 for ...

Columnist Shalom Lim reflects on how he and his late brother, Isaac, left their mark on the Singaporean DMD community as ...

For columnist Patrick Moeschen, a teacher and wheelchair user, each school year is an opportunity for teaching students about ...

The U.S. Food and Drug Administration has granted rare pediatric disease designation to NS-050/NCNP-03, an exon-skipping Duchenne muscular dystrophy (DMD) treatment from NS Pharma. Treatments granted ...