A new study describes the use of artificial intelligence (AI) in designing a new generation of capsids, the structures that ...

D Molecular Therapeutics reported its experimental gene therapy demonstrated a nearly 90% reduction in the need for ...

Bothnia dystrophy, a hereditary form of blindness, significantly affects people in the Västerbotten region of Sweden, ...

Bothnia dystrophy is a form of hereditary blindness, prevalent in the region Västerbotten in Sweden. A new study at ...

The Swedish biotech company Cellevate has raised €3.2 million in a seed round to fuel the commercialization of its ...

In an early phase trial, gene therapy showed an ability to restore function to rods and cones as well as functional vision ...

Oxford Biomedica rebrands as OXB reinforcing transformation into leading global cell and gene therapy CDMO Oxford, UK – 18 ...

Immunosuppressants used in adeno-associated virus (AAV) gene therapy for monogenic disorders present an adverse effect ...

Co-expressing NPY and its inhibitory receptor Y2 in excitatory hippocampal cells allows inhibitory autoregulation of ...

The company said the single-arm multicenter Phase II trial may support accelerated approval for the RP-A501 gene therapy in the US.

The investigational gene-editing therapy MGX-001 for hemophilia A has shown promising safety and durability in an ongoing ...

Researchers at the Karolinska Institute continue to investigate whether gene therapy can improve vision in people with ...